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Sorry forgot to include her REAL NAME It is Gillian Andersen There is a

site on her if you go to your search program and type in neurofibromatosis

Marnie

At 12:06 AM 10/11/00 -0400, you wrote:

>Its Jillian ? from that Sci Fi show and her brother doesn't have NF2, he has

>NF1

>

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Sorry forgot to include her REAL NAME It is Gillian Andersen There is a

site on her if you go to your search program and type in neurofibromatosis

Marnie

At 12:06 AM 10/11/00 -0400, you wrote:

>Its Jillian ? from that Sci Fi show and her brother doesn't have NF2, he has

>NF1

>

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Gillian ;her brother has NF1 and she is connected to NF Inc. She

does a lot, but again, her brother has NF1.

Marie

Clinical trials

>> >>

>> >>

>> >>> Dear Marie,

>> >>>

>> >>>

>> >>> There is also a lot of trials associated with various institutions

that

>> are

>> >>> not listed here. Europe as well. I find it illuminating as to what

they

>> are

>> >>> still trying to establish....or beginning to consider. That's why I

>> thought

>> >>> we should have a database and pass on a lot of this info......and

>> perhaps

>> >>> save some time.

>> >>> After Barbara's post of those drugs, I started to look at the big

drug

>> >>> companies and their research and where they are heading.....

>> >>> I found Myriad Genetics an interesting company and was a little

alarmed

>> to

>> >>> see they hold patents on genes. They have explained to me that you

can

>> only

>> >>> hold a patent on a small identified function(or dysfunction) of a

gene.

>> >>> (They have the patent to BRCA1). I suppose that Celera has the Nf2

gene,

>> >> I'm

>> >>> guessing.Perhaps this just means that anybody who finds a pathway of

>> drug

>> >> or

>> >>> gene therapy has to pay out a lot of money to whoever holds the

>> >>> patent.....Still so much to learn..

>> >>> Can't find any company so far focusing on a specific therapy for us

>> >>> though..... However am getting responses from them and always believe

in

>> >>> lobbying people.

>> >>> I would think that if we could get a drug company to undertake

>> specific

>> >>> research into a therapy, we would see a result sooner (durr)...

>> >>>

>> >>> I'm still not understanding something fundamental here.....going

through

>> >> all

>> >>> the gene therapy trials(see Medscape gene therapy trials) that have

been

>> >>> undertaken with various disorders (with mixed results!), I wonder why

>> >> these

>> >>> disorders have reached this point and NF has not.........where are

we

>> in

>> >>> the " pipeline'? Are we in any pipeline? I understand that the

disorders

>> >> that

>> >>> involve more than one chromosome are much more complicated, but this

>> isn't

>> >>> our problem..

>> >>> Whilst some of these drugs that are mentioned may be relevant to

NF2,

>> it

>> >>> would be better if they had been developed with Nf2 in mind...

>> >>>

>> >>> Any more clues, I look forward to reading your posts and how they

>> >> illuminate

>> >>> me.

>> >>> Rosemary.

>> >>>

>> >>>

>> >>>

>> >>>

>> >>>

>> >>>

>> >>>

>> >>>

>> >>>

>> >>>

>> >>

>> >>

>> >>

>> >Marie, I'm so pleased you said that....after being initially surprised

and

>> >heartened by the amount of research dollars going into NF1 and 2

research,

>> >I became increasingly frustrated with the lack of development of

>> therapies.

>> >Who do we lobby?What can we do? Rosemary.

>> >

>> >

>> >

>> >

>> >

>> >

>

>

>

>

>

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Share on other sites

Gillian ;her brother has NF1 and she is connected to NF Inc. She

does a lot, but again, her brother has NF1.

Marie

Clinical trials

>> >>

>> >>

>> >>> Dear Marie,

>> >>>

>> >>>

>> >>> There is also a lot of trials associated with various institutions

that

>> are

>> >>> not listed here. Europe as well. I find it illuminating as to what

they

>> are

>> >>> still trying to establish....or beginning to consider. That's why I

>> thought

>> >>> we should have a database and pass on a lot of this info......and

>> perhaps

>> >>> save some time.

>> >>> After Barbara's post of those drugs, I started to look at the big

drug

>> >>> companies and their research and where they are heading.....

>> >>> I found Myriad Genetics an interesting company and was a little

alarmed

>> to

>> >>> see they hold patents on genes. They have explained to me that you

can

>> only

>> >>> hold a patent on a small identified function(or dysfunction) of a

gene.

>> >>> (They have the patent to BRCA1). I suppose that Celera has the Nf2

gene,

>> >> I'm

>> >>> guessing.Perhaps this just means that anybody who finds a pathway of

>> drug

>> >> or

>> >>> gene therapy has to pay out a lot of money to whoever holds the

>> >>> patent.....Still so much to learn..

>> >>> Can't find any company so far focusing on a specific therapy for us

>> >>> though..... However am getting responses from them and always believe

in

>> >>> lobbying people.

>> >>> I would think that if we could get a drug company to undertake

>> specific

>> >>> research into a therapy, we would see a result sooner (durr)...

>> >>>

>> >>> I'm still not understanding something fundamental here.....going

through

>> >> all

>> >>> the gene therapy trials(see Medscape gene therapy trials) that have

been

>> >>> undertaken with various disorders (with mixed results!), I wonder why

>> >> these

>> >>> disorders have reached this point and NF has not.........where are

we

>> in

>> >>> the " pipeline'? Are we in any pipeline? I understand that the

disorders

>> >> that

>> >>> involve more than one chromosome are much more complicated, but this

>> isn't

>> >>> our problem..

>> >>> Whilst some of these drugs that are mentioned may be relevant to

NF2,

>> it

>> >>> would be better if they had been developed with Nf2 in mind...

>> >>>

>> >>> Any more clues, I look forward to reading your posts and how they

>> >> illuminate

>> >>> me.

>> >>> Rosemary.

>> >>>

>> >>>

>> >>>

>> >>>

>> >>>

>> >>>

>> >>>

>> >>>

>> >>>

>> >>>

>> >>

>> >>

>> >>

>> >Marie, I'm so pleased you said that....after being initially surprised

and

>> >heartened by the amount of research dollars going into NF1 and 2

research,

>> >I became increasingly frustrated with the lack of development of

>> therapies.

>> >Who do we lobby?What can we do? Rosemary.

>> >

>> >

>> >

>> >

>> >

>> >

>

>

>

>

>

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Share on other sites

Gillian ;her brother has NF1 and she is connected to NF Inc. She

does a lot, but again, her brother has NF1.

Marie

Clinical trials

>> >>

>> >>

>> >>> Dear Marie,

>> >>>

>> >>>

>> >>> There is also a lot of trials associated with various institutions

that

>> are

>> >>> not listed here. Europe as well. I find it illuminating as to what

they

>> are

>> >>> still trying to establish....or beginning to consider. That's why I

>> thought

>> >>> we should have a database and pass on a lot of this info......and

>> perhaps

>> >>> save some time.

>> >>> After Barbara's post of those drugs, I started to look at the big

drug

>> >>> companies and their research and where they are heading.....

>> >>> I found Myriad Genetics an interesting company and was a little

alarmed

>> to

>> >>> see they hold patents on genes. They have explained to me that you

can

>> only

>> >>> hold a patent on a small identified function(or dysfunction) of a

gene.

>> >>> (They have the patent to BRCA1). I suppose that Celera has the Nf2

gene,

>> >> I'm

>> >>> guessing.Perhaps this just means that anybody who finds a pathway of

>> drug

>> >> or

>> >>> gene therapy has to pay out a lot of money to whoever holds the

>> >>> patent.....Still so much to learn..

>> >>> Can't find any company so far focusing on a specific therapy for us

>> >>> though..... However am getting responses from them and always believe

in

>> >>> lobbying people.

>> >>> I would think that if we could get a drug company to undertake

>> specific

>> >>> research into a therapy, we would see a result sooner (durr)...

>> >>>

>> >>> I'm still not understanding something fundamental here.....going

through

>> >> all

>> >>> the gene therapy trials(see Medscape gene therapy trials) that have

been

>> >>> undertaken with various disorders (with mixed results!), I wonder why

>> >> these

>> >>> disorders have reached this point and NF has not.........where are

we

>> in

>> >>> the " pipeline'? Are we in any pipeline? I understand that the

disorders

>> >> that

>> >>> involve more than one chromosome are much more complicated, but this

>> isn't

>> >>> our problem..

>> >>> Whilst some of these drugs that are mentioned may be relevant to

NF2,

>> it

>> >>> would be better if they had been developed with Nf2 in mind...

>> >>>

>> >>> Any more clues, I look forward to reading your posts and how they

>> >> illuminate

>> >>> me.

>> >>> Rosemary.

>> >>>

>> >>>

>> >>>

>> >>>

>> >>>

>> >>>

>> >>>

>> >>>

>> >>>

>> >>>

>> >>

>> >>

>> >>

>> >Marie, I'm so pleased you said that....after being initially surprised

and

>> >heartened by the amount of research dollars going into NF1 and 2

research,

>> >I became increasingly frustrated with the lack of development of

>> therapies.

>> >Who do we lobby?What can we do? Rosemary.

>> >

>> >

>> >

>> >

>> >

>> >

>

>

>

>

>

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You mention Myriad Genetics. One of the people closely involved with Myriad

is Mark Skolnick and it is he who identified Chromosome 17 as the one on

which the gene for Nf1 is found. He attended a conference in England that

was organised by the Nf Association to which one of the other delegates had

brought his computer with a 'chromosome deletion map'. One evening, after a

good meal, all the delegates pooled their knowledge based on research each

one was carrying out to find the right chromosome and slowly the chromosomes

were filled up. Mark was particularly happy that night because it filled in

some of the data he was missing and it was only six weeks later that he made

the announcement.

He is now involved with Myriad and the patenting of human genes. It is

true, they have a patent on BRCA1 in the US. Three years ago I was involved

in trying to stop the patenting of genes being allowed in Europe but

unfortunately the Bill went through and it looks like they are going to be

able to patent them over here. This probably means that only a few

laboratories in Europe are going to be able to test for BRCA1 - under

licence to Myriad and Myriad taking royalties for each test - but the

majority will have to be done in the States. The figure for England that I

have heard quoted is about $2,400 per test. At the moment, with the gene

not patented, the test costs about $800. And this is just the beginning.

As far as drugs for Nf2 are concerned, there are certainly two drugs which

are nearing trial stage which may be useful but until the trials are started

it is impossible to say whether they will live up to expectations. We in

the UK are probably going to be involved in the trials and we have meetings

planned for next month with one of the companies who produce one of the

drugs. But the main thing is not to build up too many hopes at the moment.

As soon as anything positive comes along, you will all be the first to know.

Hope this helps.

a

Dear Marie,

There is also a lot of trials associated with various institutions that are

not listed here. Europe as well. I find it illuminating as to what they are

still trying to establish....or beginning to consider. That's why I thought

we should have a database and pass on a lot of this info......and perhaps

save some time.

After Barbara's post of those drugs, I started to look at the big drug

companies and their research and where they are heading.....

I found Myriad Genetics an interesting company and was a little alarmed to

see they hold patents on genes. They have explained to me that you can only

hold a patent on a small identified function(or dysfunction) of a gene.

(They have the patent to BRCA1). I suppose that Celera has the Nf2 gene, I'm

guessing.Perhaps this just means that anybody who finds a pathway of drug or

gene therapy has to pay out a lot of money to whoever holds the

patent.....Still so much to learn..

Can't find any company so far focusing on a specific therapy for us

though..... However am getting responses from them and always believe in

lobbying people.

I would think that if we could get a drug company to undertake specific

research into a therapy, we would see a result sooner (durr)...

I'm still not understanding something fundamental here.....going through all

the gene therapy trials(see Medscape gene therapy trials) that have been

undertaken with various disorders (with mixed results!), I wonder why these

disorders have reached this point and NF has not.........where are we in

the " pipeline'? Are we in any pipeline? I understand that the disorders that

involve more than one chromosome are much more complicated, but this isn't

our problem..

Whilst some of these drugs that are mentioned may be relevant to NF2, it

would be better if they had been developed with Nf2 in mind...

Any more clues, I look forward to reading your posts and how they illuminate

me.

Rosemary.

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You mention Myriad Genetics. One of the people closely involved with Myriad

is Mark Skolnick and it is he who identified Chromosome 17 as the one on

which the gene for Nf1 is found. He attended a conference in England that

was organised by the Nf Association to which one of the other delegates had

brought his computer with a 'chromosome deletion map'. One evening, after a

good meal, all the delegates pooled their knowledge based on research each

one was carrying out to find the right chromosome and slowly the chromosomes

were filled up. Mark was particularly happy that night because it filled in

some of the data he was missing and it was only six weeks later that he made

the announcement.

He is now involved with Myriad and the patenting of human genes. It is

true, they have a patent on BRCA1 in the US. Three years ago I was involved

in trying to stop the patenting of genes being allowed in Europe but

unfortunately the Bill went through and it looks like they are going to be

able to patent them over here. This probably means that only a few

laboratories in Europe are going to be able to test for BRCA1 - under

licence to Myriad and Myriad taking royalties for each test - but the

majority will have to be done in the States. The figure for England that I

have heard quoted is about $2,400 per test. At the moment, with the gene

not patented, the test costs about $800. And this is just the beginning.

As far as drugs for Nf2 are concerned, there are certainly two drugs which

are nearing trial stage which may be useful but until the trials are started

it is impossible to say whether they will live up to expectations. We in

the UK are probably going to be involved in the trials and we have meetings

planned for next month with one of the companies who produce one of the

drugs. But the main thing is not to build up too many hopes at the moment.

As soon as anything positive comes along, you will all be the first to know.

Hope this helps.

a

Dear Marie,

There is also a lot of trials associated with various institutions that are

not listed here. Europe as well. I find it illuminating as to what they are

still trying to establish....or beginning to consider. That's why I thought

we should have a database and pass on a lot of this info......and perhaps

save some time.

After Barbara's post of those drugs, I started to look at the big drug

companies and their research and where they are heading.....

I found Myriad Genetics an interesting company and was a little alarmed to

see they hold patents on genes. They have explained to me that you can only

hold a patent on a small identified function(or dysfunction) of a gene.

(They have the patent to BRCA1). I suppose that Celera has the Nf2 gene, I'm

guessing.Perhaps this just means that anybody who finds a pathway of drug or

gene therapy has to pay out a lot of money to whoever holds the

patent.....Still so much to learn..

Can't find any company so far focusing on a specific therapy for us

though..... However am getting responses from them and always believe in

lobbying people.

I would think that if we could get a drug company to undertake specific

research into a therapy, we would see a result sooner (durr)...

I'm still not understanding something fundamental here.....going through all

the gene therapy trials(see Medscape gene therapy trials) that have been

undertaken with various disorders (with mixed results!), I wonder why these

disorders have reached this point and NF has not.........where are we in

the " pipeline'? Are we in any pipeline? I understand that the disorders that

involve more than one chromosome are much more complicated, but this isn't

our problem..

Whilst some of these drugs that are mentioned may be relevant to NF2, it

would be better if they had been developed with Nf2 in mind...

Any more clues, I look forward to reading your posts and how they illuminate

me.

Rosemary.

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Share on other sites

You mention Myriad Genetics. One of the people closely involved with Myriad

is Mark Skolnick and it is he who identified Chromosome 17 as the one on

which the gene for Nf1 is found. He attended a conference in England that

was organised by the Nf Association to which one of the other delegates had

brought his computer with a 'chromosome deletion map'. One evening, after a

good meal, all the delegates pooled their knowledge based on research each

one was carrying out to find the right chromosome and slowly the chromosomes

were filled up. Mark was particularly happy that night because it filled in

some of the data he was missing and it was only six weeks later that he made

the announcement.

He is now involved with Myriad and the patenting of human genes. It is

true, they have a patent on BRCA1 in the US. Three years ago I was involved

in trying to stop the patenting of genes being allowed in Europe but

unfortunately the Bill went through and it looks like they are going to be

able to patent them over here. This probably means that only a few

laboratories in Europe are going to be able to test for BRCA1 - under

licence to Myriad and Myriad taking royalties for each test - but the

majority will have to be done in the States. The figure for England that I

have heard quoted is about $2,400 per test. At the moment, with the gene

not patented, the test costs about $800. And this is just the beginning.

As far as drugs for Nf2 are concerned, there are certainly two drugs which

are nearing trial stage which may be useful but until the trials are started

it is impossible to say whether they will live up to expectations. We in

the UK are probably going to be involved in the trials and we have meetings

planned for next month with one of the companies who produce one of the

drugs. But the main thing is not to build up too many hopes at the moment.

As soon as anything positive comes along, you will all be the first to know.

Hope this helps.

a

Dear Marie,

There is also a lot of trials associated with various institutions that are

not listed here. Europe as well. I find it illuminating as to what they are

still trying to establish....or beginning to consider. That's why I thought

we should have a database and pass on a lot of this info......and perhaps

save some time.

After Barbara's post of those drugs, I started to look at the big drug

companies and their research and where they are heading.....

I found Myriad Genetics an interesting company and was a little alarmed to

see they hold patents on genes. They have explained to me that you can only

hold a patent on a small identified function(or dysfunction) of a gene.

(They have the patent to BRCA1). I suppose that Celera has the Nf2 gene, I'm

guessing.Perhaps this just means that anybody who finds a pathway of drug or

gene therapy has to pay out a lot of money to whoever holds the

patent.....Still so much to learn..

Can't find any company so far focusing on a specific therapy for us

though..... However am getting responses from them and always believe in

lobbying people.

I would think that if we could get a drug company to undertake specific

research into a therapy, we would see a result sooner (durr)...

I'm still not understanding something fundamental here.....going through all

the gene therapy trials(see Medscape gene therapy trials) that have been

undertaken with various disorders (with mixed results!), I wonder why these

disorders have reached this point and NF has not.........where are we in

the " pipeline'? Are we in any pipeline? I understand that the disorders that

involve more than one chromosome are much more complicated, but this isn't

our problem..

Whilst some of these drugs that are mentioned may be relevant to NF2, it

would be better if they had been developed with Nf2 in mind...

Any more clues, I look forward to reading your posts and how they illuminate

me.

Rosemary.

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Jimmy,

we're looking for someone famous, not infamous!

>>It has been said that

>if we had a " name " -be it an athlete, actor, politician--who had NF2, then

>you would have people asking--what is Nf2, etc. far aAs s who to

.........................................................................

ummm,cough,cough,uhuhuh umm.Need I remind you,you got ME........JIMMY!!!<<

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Jimmy,

we're looking for someone famous, not infamous!

>>It has been said that

>if we had a " name " -be it an athlete, actor, politician--who had NF2, then

>you would have people asking--what is Nf2, etc. far aAs s who to

.........................................................................

ummm,cough,cough,uhuhuh umm.Need I remind you,you got ME........JIMMY!!!<<

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Jimmy,

we're looking for someone famous, not infamous!

>>It has been said that

>if we had a " name " -be it an athlete, actor, politician--who had NF2, then

>you would have people asking--what is Nf2, etc. far aAs s who to

.........................................................................

ummm,cough,cough,uhuhuh umm.Need I remind you,you got ME........JIMMY!!!<<

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  • 2 weeks later...

I know you didn't really mean " too bad MJF has parkinsons " , but it sure

sounded weird!. .Both diseases are quite a burden to bear. . and I don't

think any of us would wish either of them on anyone! !

In a message dated 10/10/2000 9:48:28 PM Eastern Daylight Time, mcdrew@...

writes:

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I know you didn't really mean " too bad MJF has parkinsons " , but it sure

sounded weird!. .Both diseases are quite a burden to bear. . and I don't

think any of us would wish either of them on anyone! !

In a message dated 10/10/2000 9:48:28 PM Eastern Daylight Time, mcdrew@...

writes:

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I know you didn't really mean " too bad MJF has parkinsons " , but it sure

sounded weird!. .Both diseases are quite a burden to bear. . and I don't

think any of us would wish either of them on anyone! !

In a message dated 10/10/2000 9:48:28 PM Eastern Daylight Time, mcdrew@...

writes:

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